TrialNCT05175105Phase 3Active not recruiting
A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period
Study sponsor: Agios Pharmaceuticals, Inc. · AGIO
Compare the available registry edits below. Primary completion is the date data collection ends for the main study measures; it does not tell you when results will be published.
Primary completion2024-12-13Actual
Enrollment · participants30Actual
Source updated2026-08-27Last update listed in the registry record
Version history
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