NCT04729751Phase 2Completed

A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).

Study sponsor: Mirum Pharmaceuticals, Inc. · MIRM

Compare the available registry edits below. Primary completion is the date data collection ends for the main study measures; it does not tell you when results will be published.

Primary completion2024-12-17Actual
Enrollment · participants27Actual
Source updated2026-06-02Last update listed in the registry record
Version history

Changes to this trial

Last 12 months
Pro unlocks the full available history and CSV export. View Pro features

· 1 field changed

Primary outcomes · main study measures

Text edit · unverified significance
− Previous value

measure: Frequency of treatment-emergent adverse events [TEAEs]

+ Updated value

measure: Frequency of Treatment-emergent Adverse Events [TEAEs]

The saved outcome text may be shortened. Check the source for full wording.

Check registry source